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290 Extending the success of elexacaftor-tezacaftor-ivacaftor to rare mutations—insights from CFTR structure and modulator binding

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Year: 2023
Type: article
Source: Journal of Cystic Fibrosis
DOI: 10.1016/s1569-1993(23)01217-1
Authors: B. Kerem, N. Stanleigh, M. Gur, E. Kerem, M. Wilschanski
Institutions: Hebrew University of Jerusalem, Stanford University, Technion – Israel Institute of Technology, Rambam Health Care Campus, Hadassah Medical Center
Language: English

Topic: Cystic Fibrosis Research Advances
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: National Institutes of Health, National Institute of General Medical Sciences
Awards: The ubiquitin proteasome system in ER quality control, G8755052572
OpenAlex ID: W4387746829
FWCI:
Cites: 4
Cited by:
Related to: 10
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