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Luspatercept for the Treatment of Anemia in Non-Transfusion-Dependent β-Thalassemia: Final Safety and Efficacy Data from the BEYOND Trial

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Year: 2023
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2023-174097
Authors: Ali T Taher, Vip Viprakasit, Antonis Kattamis, Silverio Perrotta, Paolo Ricchi, John B. Porter, Thomas D Coates, Gian Luca Forni, Khaled M. Musallam, Oriana Esposito, Ana Carolina Giuseppi, Wen-Ling Kuo, Marta Reverte, Richard Wei, Luciana Moro Bueno, Maria Domenica Cappellini
Institutions: American University of Beirut Medical Center, Mahidol University, National and Kapodistrian University of Athens, University of Campania "Luigi Vanvitelli", University College London, University of Southern California, Children's Hospital Los Angeles, Ente Ospedaliero Ospedali Galliera, Bristol-Myers Squibb (Switzerland), Bristol-Myers Squibb (United States), University of Milan, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4389234939
Cites:
Cited by: 5
Related to: 10
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