DUX4 siRNA Optimization for the Development of an Antibody-Oligonucleotide Conjugate (AOC) for the Treatment of FSHD (P17-13.009)
Year: 2022
Type: article
Source: Neurology
Authors: Barbora Malecova, David Sala, Garineh Mary Melikian, Gulin Erdogan, Rachel Johns, Joanne Young, Erwann Ventre, Sole Gatto, Matthew Onorato, Adam Pavlicek, Orsolya Kiraly, Martin Koegler, Arthur A. Levin, Philipp Hadwiger, Mike Flanagan, Mark Stahl
Institutions: Avidity (United States), Jackson Laboratory
Language: English
Subfield: Molecular Biology
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4389374200
