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Impact of Patisiran on Activities of Daily Living and Functional Status in hATTR Amyloidosis (1493)

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Year: 2021
Type: article
Source: Neurology
DOI: 10.1212/wnl.96.15_supplement.1493
Authors: Amanda Peltier, Alejandra Gonzalez-Duarte, John Berk, Ivailo Tournev, Ole Suhr, Senda Ajroud-Driss, Madeline Merkel, Hollis Lin, Cecilia Hale, David Adams
Institutions: Vanderbilt University, Instituto Nacional de Ciencias Médicas y Nutrición Salvador Zubirán, Boston University, Alexandrovska Hospital, Umeå University, Northwestern University, Alnylam Pharmaceuticals (United States)
Language: English

Topic: Amyloidosis: Diagnosis, Treatment, Outcomes
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4389447260
FWCI: 0.079
Cites:
Cited by: 1
Related to: 10
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