Design of a Phase 3, Randomized, Placebo-controlled Trial of Tofersen Initiated in Clinically Pre-symptomatic SOD1 Mutation Carriers with a Longitudinal Natural History Run-in (2285)
Year: 2021
Type: article
Study design: Study Protocol
Source: Neurology
Authors: Michael Benatar, Joanne Wuu, Peter M. Andersen, Jinsy Andrews, Robert C. Bucelli, Markus Otto, Toby A. Ferguson, Weiping Chen, Laura Fanning, Danielle Graham, Peng Sun, Yingying Liu, Janice Wong, Stephanie Fradette
Language: English
Subfield: Neurology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4389449596
