Work

CSTB gene replacement improves neuroinflammation, neurodegeneration and ataxia in murine type 1 progressive myoclonus epilepsy

Year: 2023

Type: article

Source: Gene Therapy

DOI: 10.1038/s41434-023-00433-x

Authors: Emrah Gumusgoz, Sahba Kasiri, Mayank Verma, Jun Wu, Daniel Villarreal Acha, Ummay Marriam, Sharyl Fyffe-Maricich, Amy Lin, Xin Chen, Steven J. Gray, Berge A. Minassian

Institutions: The University of Texas Southwestern Medical Center, Ultragenyx Pharmaceutical (United States)

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4390112364

FWCI: 0.44

Cites: 43

Cited by: 3

Related to: 10