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Bleeding Outcomes in Participants with Factor VIII Activity<5 IU/dL post–gene transfer in GENEr8-1

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Year: 2024
Type: conference-paper
Source: Hämostaseologie
DOI: 10.1055/s-0044-1779110
Authors: J. Mahlangu, M. Ozelo, C. W. Tan, A. Giermasz, J.-D. Wang, S. Harris, D. Osmond, H. Yu, T. Robinson
Institutions: National Health Laboratory Service, University of the Witwatersrand, Johannesburg Hospital, Universidade Estadual de Campinas (UNICAMP), Royal Adelaide Hospital, The University of Adelaide, University of California Davis Medical Center, University of California, Davis, Taichung Veterans General Hospital, BioMarin (United States)
Language: English

Topic: Hemophilia Treatment and Research
Subfield: Hematology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4392664694
FWCI:
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Cited by:
Related to: 10
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