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Liposome-encapsulated mannose-1-phosphate therapy improves global N-glycosylation in different congenital disorders of glycosylation

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Year: 2024
Type: article
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2024.108487
Authors: Rohit Budhraja, Silvia Radenkovic, Anu Jain, Irena J.J. Muffels, Moulay Hicham Alaoui Ismaili, Tamas Kozicz, Akhilesh Pandey, Eva Morava
Institutions: Mayo Clinic, Icahn School of Medicine at Mount Sinai, Glycomine, Inc. (United States), University of Pecs, Manipal Academy of Higher Education
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: University of Minnesota, Rare Diseases Clinical Research Network, National Institutes of Health, National Institute of Neurological Disorders and Stroke, National Institute of Child Health and Human Development, National Center for Advancing Translational Sciences
Awards: G7300629457, G8762761747, G9000051534
OpenAlex ID: W4396691048
FWCI: 4.487
Cites: 42
Cited by: 19
Related to: 10
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