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Doubling down on PK activation for sickle cell disease

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Year: 2024
Type: article
Source: Blood Advances
DOI: 10.1182/bloodadvances.2024013367
Authors: Samuel R. Wilson, Lydia H. Pecker
Institutions: University of North Carolina at Chapel Hill, Johns Hopkins University, Johns Hopkins Medicine
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: gold
Estimated APC paid: $3,000

Funders: Andrew W. Mellon Foundation, Alexion Pharmaceuticals, Agios Pharmaceuticals, Novo Nordisk, National Institutes of Health, National Heart, Lung, and Blood Institute
Awards: OVARIAN RESERVE IN POST-MENARCHAL FEMALES WITH SICKLE CELL ANEMIA, Clinical and genetic risk factors associated with adverse long-term health outcomes after curative therapies in individuals with sickle cell disease
OpenAlex ID: W4401909515
FWCI:
Cites: 8
Cited by:
Related to: 10
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