259 Splice-switching antisense oligonucleotides to recover CFTR function disrupted by C-terminal truncating nucleotide variants
Year: 2024
Type: article
Source: Journal of Cystic Fibrosis
Language: English
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
Open Access status: bronze
OpenAlex ID: W4402235214
