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Assessment of non-myelotoxic agents as a preparatory regimen for hematopoietic stem cell gene therapy

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Year: 2024
Type: article
Source: Human Cell
DOI: 10.1007/s13577-024-01130-6
Authors: Mehmet Emin Şeker, Özgür Doğuş Erol, Burcu Pervin, Gerard Wagemaker, Niek P. van Til, Fatima Aerts-Kaya
Institutions: Hacettepe University, Erasmus University Rotterdam, Emma Kinderziekenhuis, Amsterdam Neuroscience, Amsterdam University Medical Centers, Vrije Universiteit Amsterdam
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: green

Funders: Ankara Universitesi, European Commission, Türkiye Bilimsel ve Teknolojik Araştırma Kurumu, Hacettepe Üniversitesi
Awards: G3135116822, G5332591001, G6246278550, G6265637710, G7016759175, Advanced Cell-based Therapies for the treatment of Primary ImmunoDeficiency
OpenAlex ID: W4403785668
FWCI: 0.485
Cites: 55
Cited by: 2
Related to: 10
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