The impact of nusinersen on respiratory function in adult patients with spinal muscular atrophy after 1.5 years of treatment.
Year: 2024
Type: conference-abstract
Authors: Pija Pukšič Šimek, Manca Groznik Tratnjek, Blaž Koritnik, Lea Leonardis
Institution: Ljubljana University Medical Centre
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4404090778
