Safety update: risdiplam clinical trial program for spinal muscular atrophy
Year: 2024
Type: conference-paper
Institutions: Roche (United Kingdom), Fondazione IRCCS Istituto Neurologico Carlo Besta, NIHR Great Ormond Street Hospital Biomedical Research Centre, Columbia University Irving Medical Center, University of Liège, University of Oxford, Hôpital Armand-Trousseau, Assistance Publique – Hôpitaux de Paris, Institut de Myologie, Centre Hospitalier Universitaire de Liège, Boston Children's Hospital, Harvard University, Stanford University
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4404183330
