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Safety update: risdiplam clinical trial program for spinal muscular atrophy

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Year: 2024
Type: conference-paper
DOI: 10.1136/jnnp-2024-abn.159
Authors: Yeung Wai Yin, Baranello Giovanni, Chiriboga Claudia A, Servais Laurent, Darras Basil T, Day John W, Mercuri Eugenio
Institutions: Roche (United Kingdom), Fondazione IRCCS Istituto Neurologico Carlo Besta, NIHR Great Ormond Street Hospital Biomedical Research Centre, Columbia University Irving Medical Center, University of Liège, University of Oxford, Hôpital Armand-Trousseau, Assistance Publique – Hôpitaux de Paris, Institut de Myologie, Centre Hospitalier Universitaire de Liège, Boston Children's Hospital, Harvard University, Stanford University
Language: English

Topic: Neurogenetic and Muscular Disorders Research
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4404183330
FWCI:
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Related to: 10
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