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Practical use of risdiplam (EVRYSDI▾) in Individuals with Spinal muscular atrophy

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Year: 2024
Type: conference-paper
DOI: 10.1136/jnnp-2024-abn.180
Authors: Hewamadduma Channa, Baranello Giovanni, Marini-Bettolo Chiara, Borrelli Osvaldo, Hoyle Natasha, Mangera Altaf, Martinez Anna E, Raslan Zaher, Scoto Mariacristina
Institutions: Royal Hallamshire Hospital, University of Sheffield, University College London, Great Ormond Street Hospital, Great Ormond Street Hospital for Children NHS Foundation Trust, Roche (United Kingdom)
Language: English

Topic: Neurogenetic and Muscular Disorders Research
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4404183407
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Related to: 10
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