Valoctocogene Roxaparvovec Estimated Long-Term Durability of Treatment Effect: An Extrapolation of the Most Recent Clinical Data
Year: 2024
Type: conference-abstract
Source: Blood
Authors: Sandra Santos, Tara M. Robinson, David Trueman
Institutions: BioMarin (United Kingdom), BioMarin (United States)
Language: English
Subfield: Hematology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4405038578
