Betibeglogene Autotemcel (beti-cel) Gene Addition Therapy Results in Durable Hemoglobin a Production with up to 10 Years of Follow-up with Transfusion-Dependent β-Thalassemia
Year: 2024
Type: conference-abstract
Source: Blood
Authors: Alexis Thompson, Janet L. Kwiatkowski, Jennifer Schneiderman, Isabelle Thuret, Andreas E. Kulozik, Evangelia Yannaki, Marina Cavazzana, Suradej Hongeng, Timothy S. Olson, Martin G. Sauer, Adrian J. Thrasher, Ashutosh Lal, John E. J. Rasko, Shamshad Ali, Ge Tao, Himal L. Thakar, Ami Deora, Clark Paramore, Niki Witthuhn, Mark C. Walters, Franco Locatelli
Institutions: Children's Hospital of Philadelphia, University of Pennsylvania, Northwestern University, Lurie Children's Hospital, Hôpital de la Timone, Heidelberg University, G. Papanikolaou General Hospital, Hôpital Necker-Enfants Malades, Inserm, Assistance Publique – Hôpitaux de Paris, Institut des Maladies Génétiques Imagine, Université Paris Descartes, Mahidol University, Ramathibodi Hospital, Medizinische Hochschule Hannover, University College London, UCSF Benioff Children's Hospital, The University of Sydney, Royal Prince Alfred Hospital, Centenary Institute, Università Cattolica del Sacro Cuore, Bambino Gesù Children's Hospital
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4405040405