Targeted Non-Viral Gene Delivery through Transcutaneous Ultrasound Enables Robust, Redosable, Titratable, and Durable FVIII and FIX Gene Expression in the Liver in Murine Models
Year: 2024
Type: conference-abstract
Source: Blood
Authors: Surabhi Rao, Victor Foster, Charles Levine, Bert Frederich, Jonathan Chan, Barry Campbell, Glenda Arauz, Celia Ortiz, Adel Alonso, Oliver Chen, Tanaya Ghosh, Charlotte He, Elizabeth Del Greco, David Satyadi, Anagha Rao, David Kim, Dhruv Bole, Katelyn N Benthall, Margarita Krivega, Julia Poniatowski, Ivan Krivega, Zoya Gulzman-Poltorak, Steve Feinstein, Kenneth Greenberg
Language: English
Subfield: Biomedical Engineering
Field: Engineering
Domain: Physical Sciences
Open Access status: closed
OpenAlex ID: W4405041760
