Work

Unlocking the potential of allele-specific siRNA therapy: A novel approach for Crouzon syndrome

Year: 2025

Type: article

Abstract: Publisher of over 50 scientific journals across the life, physical, earth, and health sciences, both independently and in partnership with scientific societies including Cell, Neuron, Immunity, Current Biology, AJHG, and the Trends Journals.

Source: Molecular Therapy — Nucleic Acids

DOI: 10.1016/j.omtn.2025.102484

Authors: Federico Di Rocco, Camilla de Laurentis

Institutions: Lyon 1 Université, Inserm, Hôpital Femme Mère Enfant, Hospices Civils de Lyon

Language: English

Topic: RNA Interference and Gene Delivery

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: gold

Estimated APC paid: $3,900