Systemic AAV Gene Therapy Using a CNS-targeted Engineered Capsid Significantly Increases GCase Activity to Support the Potential Treatment of PD-GBA (S37.007)
Year: 2025
Type: article
Source: Neurology
Authors: Reed Ressler, Kimberly McDowell, Brandon Wheeler, Shelby Thomas, Lubov Grigoryeva, Alexander Armendariz, Maeve Flynn, Hari Acharya, Paul Denis, Pasha Tchourilov, Swati Tole, Nick Goeden, Nicholas Flytzanis
Institution: Capsida Biotherapeutics (United States)
Language: English
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4409227181