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The Latest Data from Lenadogene Nolparvovec Gene Therapy Trials for Leber Hereditary Optic Neuropathy (S14.001)

Year: 2025

Type: article

Source: Neurology

DOI: 10.1212/wnl.0000000000208987

Authors: Nancy Newman, Patrick Yu-Wai-Man, Valerio Carelli, Valerie Biousse, Magali Taiel, José-Alain Sahel

Institutions: Emory University, University of Cambridge, University of Bologna, GenSight Biologics (France), University of Pittsburgh

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4409227730

FWCI:

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