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Incorporating Patient Perspectives into a Composite Score for Measuring Disease Progression in Spinocerebellar Ataxia (SCA) (P12-5.028)

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Year: 2025
Type: article
Source: Neurology
DOI: 10.1212/wnl.0000000000209084
Authors: Michele Potashman, Basia Rogula, Lauren Powell, Ellen Korol, Samuel Dickson, Suzanne Hendrix, Maggie Heinrich, Katja Rudell, Linda Abetz Webb, Melissa Beiner, Vlad Coric, Liana Rosenthal, Susan Perlman, Jeremy Schmahmann, Gilbert L’Italien
Institutions: Biohaven Pharmaceuticals (United States), Health Economics and Outcomes Research (United Kingdom), PAREXEL International (United Kingdom), PAREXEL International (United States), Johns Hopkins University, Johns Hopkins Medicine, University of California, Los Angeles, Massachusetts General Hospital
Language: English

Topic: Genetic Neurodegenerative Diseases
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4409234659
FWCI:
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Related to: 10
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