Work

SARA Eight-Item Subgroup Analysis of N-acetyl-L-leucine for Niemann-Pick Disease Type C (S27.002)

Year: 2025

Type: article

Source: Neurology

DOI: 10.1212/wnl.0000000000209037

Authors: Marc Patterson, Bethany Zanrucha, Janelle Schafer, Michael Strupp, Tatiana Bremova-Ertl, Ian Billington

Institutions: IntraBio Inc. (United States), Ludwig-Maximilians-Universität München, University Hospital of Bern

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4409235624

FWCI:

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Related to: 10