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Comparative Effectiveness of Troriluzole Versus Untreated Natural History Cohorts in Spinocerebellar Ataxia Leveraging Propensity Score Matching Methods (P6-5.012)

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Year: 2025
Type: article
Study design: Observational Study
Source: Neurology
DOI: 10.1212/wnl.0000000000209018
Authors: Gilbert L’Italien, Michele Potashman, Melissa Beiner, Basia Rogula, Lauren Powell, Victoria Wirtz, David Stock, Irfan Qureshi, Sheng-Han Kuo, Liana Rosenthal, Susan Perlman, Vlad Coric, Jeremy Schmahmann
Institutions: Biohaven Pharmaceuticals (United States), Health Economics and Outcomes Research (United Kingdom), Columbia University, Johns Hopkins University, Johns Hopkins Medicine, University of California, Los Angeles, Massachusetts General Hospital
Language: English

Topic: Genetic Neurodegenerative Diseases
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4409235829
FWCI: 0.356
Cites:
Cited by: 1
Related to: 10
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