RAG-17, a Novel siRNA Therapy for SOD1-ALS: Safety and Preliminary Efficacy from a First-in-human Trial (S5.003)
Year: 2025
Type: article
Source: Neurology
Authors: Jinyi Ye, Lingling Jiang, Ling Wang, Yuesong Pan, Xuan Wang, Hui Qu, Xiaoling Liao, Xuejiao Zhou, Shawn Zhang, Moorim Kang, Long-Cheng Li, Weiqi Chen, Yilong Wang
Institutions: Capital Medical University, Beijing Tian Tan Hospital
Language: English
Subfield: Neurology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4409237343
