Work

Sinbaglustat ameliorates disease pathology in a murine model of GM1 gangliosidosis without affecting CNS ganglioside levels

Year: 2025

Type: article

Abstract: gangliosidosis mouse model.

Source: Neurobiology of Disease

DOI: 10.1016/j.nbd.2025.106917

Authors: Rouven Wannemacher, Lorna Jubran-Rudolf, Isabel Zdora, Eva Leitzen, Karl Rohn, Virginie Sippel, Christoph Paschen, Peter Blattmann, Wolfgang Baumgärtner, Ingo Gerhauser, Michel Alexander Steiner

Institutions: University of Veterinary Medicine Hannover, Foundation, Idorsia Pharmaceuticals Ltd (Switzerland)

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: gold

Estimated APC paid: $4,180

Funders: Stiftung Tierärztliche Hochschule Hannover, Idorsia Pharmaceuticals

OpenAlex ID: W4409499847

FWCI: 4.798

Cites: 90

Cited by: 9

Related to: 10