Optimization of BTK Donor for CRISPR/Cas9 Gene Therapy of X-Linked Agammaglobulinemia (XLA)
Year: 2025
Type: article
Source: Cytotherapy
Authors: E.J. Velazquez, A. Colamartino, G. Hinojosa, D. Kohn
Institution: University of California, Los Angeles
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4409909366
