LBP-031 Advancing prime editing for Wilson disease: precise and durable in vivo Correction of ATP7B mutations
Year: 2025
Type: conference-abstract
Source: Journal of Hepatology
Authors: John Hadcock, David Waterman, Shivangi Modi, Alicia Volmar, Michelle O’Connor, Celia Chang, Justin Darcy, Chaitali Dutta, Marine Hatit, Rowshon Alam, Mallik Putta, Serge Kyrychenko, Jacob Stewart-Ornstein, Seth Alexander, Jonathan Winnay, Andrea de Erkenez, Jonathan Levy, Andrew Anzalone, mohammed asmal, Jeremy Duffield, Vivian Choi
Language: English
Subfield: Molecular Biology
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4410174691
