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Evaluating the safety profile of defibrotide in sickle cell disease: an in vitro study

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Year: 2025
Type: article
Abstract: Not available.
Source: Haematologica
DOI: 10.3324/haematol.2025.287447
Authors: Laura Bencheikh, Meghan Perkins, Kim Anh Nguyen, Clara Noizat, Anoosha Habibi, Marie Cambot, Pablo Bartolucci
Institutions: Inserm, Université Paris-Est Créteil, Établissement Français du Sang, Institut Mondor de Recherche Biomédicale, Assistance Publique – Hôpitaux de Paris, Hôpitaux Universitaires Henri-Mondor
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: gold
Estimated APC paid: $2,157

Funders: Jazz Pharmaceuticals, Agios Pharmaceuticals, Institut National de la Santé et de la Recherche Médicale
OpenAlex ID: W4410188189
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Related to: 10
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