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Engineered AAV capsids mediate transduction of murine neurofibroma and sciatic nerve

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Year: 2025
Type: article
Source: Gene Therapy
DOI: 10.1038/s41434-025-00542-9
Authors: Edwina Abou Haidar, Shilpa Prabhakar, Pike See Cheah, Killian S. Hanlon, Paula Espinoza, Adam V. Crain, Nikita Patel, Greta W. Radcliff, Ming Cheng, Iván Coto Hernández, Steven Minderler, Demitri de la Cruz, Carrie Ng, Cintia Carla da Hora, Alain Charest, Anat Stemmer-Rachamimov, Nate Jowett, Xandra O. Breakefield, Casey A. Maguire
Institutions: Harvard University, Massachusetts General Hospital, Universiti Putra Malaysia, University College London, Massachusetts Eye and Ear Infirmary, Mayo Clinic, Mayo Clinic in Florida, Beth Israel Deaconess Medical Center
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: green

Funders: U.S. Department of Health and Human Services, National Institutes of Health, National Institute on Deafness and Other Communication Disorders, National Institute of Biomedical Imaging and Bioengineering
Awards: Enhanced gene delivery for CNS and sensory disorders, G8925296879, Super-resolved multiphoton microscopy with dual output ultrafast laser
OpenAlex ID: W4411163460
FWCI: 1.167
Cites: 45
Cited by: 2
Related to: 10
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