Eltrombopag for Bone Marrow Failure in Fanconi Anemia: Results From the Phase II Clinical Trial FANCREV
Year: 2025
Type: article
Study design: Clinical Trial
Source: European Journal Of Haematology
DOI: 10.1111/ejh.70007
Authors: June Iriondo, Josune Zubicaray, Paula Río, Albert Català, María Solsona, Alejandro Sanz, Ana Gómez, Elena Sebastián, Ana de la Cruz, Almudena Galán, Susana Navarro, Lise Larcher, Nagore García de Andoin, Jose Javier Uriz, José Manuel Vagace, Jesús Gonzalez de Pablo, Maria Roser Pujol, Eileen Nicoletti, Jordi Surrallés, Silvia Martín‐Prado, Jonathan D. Schwartz, Jean Soulier, Juan Antonio Bueren, Julián Sevilla
Institutions: Centre for Biomedical Network Research on Rare Diseases, Hospital Infantil Universitario Niño Jesús, Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, Instituto de Investigación Sanitaria Fundación Jiménez Díaz, Hospital Sant Joan de Déu Barcelona, Institut de Recerca Sant Joan de Déu, Centre National de la Recherche Scientifique, Inserm, Université Paris Cité, Hôpital Saint-Louis, Institut de recherche Saint-Louis, Donostiako Unibertsitate Ospitalea, Universitat Autònoma de Barcelona, Institut de Recerca Sant Pau
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
Awards: G3828799090, G4687829006
OpenAlex ID: W4412487064
