Work

N-of-1 CHCHD10 ALS Antisense Oligonucleotide Trial Shows Early Signs of Efficacy

Year: 2025

Type: preprint

Study design: Case Report

Source: SSRN Electronic Journal

DOI: 10.2139/ssrn.5365287

Authors: Margot A. Cousin, Aditi I. Dagli, Laurence Mignon, Jaimin S. Shah, Mercedes Prudencio, Tania F. Gendron, Marka Van Blitterswijk, Erik H. Middlebrooks, Megan Donahue, Jany Dagher, Jens O. Watzlawik, Wolfdieter Springer, Zachary McEachin, Leonard Petrucelli, Bjorn Oskarsson

Institutions: Mayo Clinic, Orlando Health, Emory University, Mayo Clinic in Florida

Language: Dutch

Topic: Amyotrophic Lateral Sclerosis Research

Subfield: Neurology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: green

OpenAlex ID: W4412713994

Cites: 9

Cited by:

Related to: 10