Advancements in Nonviral Gene Editing Strategies for Rare Diseases
Year: 2025
Type: article
Source: Human Gene Therapy
Institutions: Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, Instituto de Investigación Sanitaria Fundación Jiménez Díaz, Intellia Therapeutics (United States), National Research Council, Istituto di Analisi dei Sistemi ed Informatica Antonio Ruberti, Madrid Institute for Advanced Studies, IMDEA Nanoscience
Language: English
Subfield: Molecular Biology
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4413970641
