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Advancements in Nonviral Gene Editing Strategies for Rare Diseases

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Year: 2025
Type: article
Source: Human Gene Therapy
DOI: 10.1177/10430342251372056
Authors: Jimena Pérez-Maroto, Laura Sepp-Lorenzino, Diego Castaño-Esteban, Daniela Palacios, Begoña Sot
Institutions: Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas, Instituto de Investigación Sanitaria Fundación Jiménez Díaz, Intellia Therapeutics (United States), National Research Council, Istituto di Analisi dei Sistemi ed Informatica Antonio Ruberti, Madrid Institute for Advanced Studies, IMDEA Nanoscience
Language: English

Topic: RNA Interference and Gene Delivery
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4413970641
FWCI: 1.015
Cites: 148
Cited by: 4
Related to: 10
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