Work

Efficacy and Safety of Olipudase Alfa for the Treatment of Acid Sphingomyelinase Deficiency ( ASMD ): A Systematic Review and Meta‐Analysis

Year: 2025

Type: review

Study designs: Systematic Review, Meta-Analysis

Source: American Journal of Medical Genetics Part A

DOI: 10.1002/ajmg.a.64258

Authors: Breno Bopp Antonello, Giovanna Giovacchini, Anna Luiza Braga Albuquerque, Cainã Gonçalves Rodrigues, Laura Grespan Dill, Maria Inez Dacoregio, Paulo Victor Zattar Ribeiro

Institutions: Universidade Franciscana, Faculdade de Medicina do ABC, Universidade Federal de Minas Gerais, Universidade Federal do Ceará, Universidade Federal de Santa Maria, Universidade de São Paulo

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4414377868

FWCI: 0.388

Cites: 25

Cited by: 2

Related to: