Study of trofinetide in Rett syndrome: Lessons from an approved drug for a severe neurodevelopmental disorder
Year: 2025
Type: article
DOI: 10.1111/dmcn.70025
Author: Walter E. Kaufmann
Institutions: Boston Children's Hospital, Emory University
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4414525452
