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Supporting Patient‐Centred Decisions on Gene Therapy for Haemophilia A: A Conceptual Model

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Year: 2025
Type: article
Source: Haemophilia
DOI: 10.1111/hae.70136
Authors: Giovanni Di Minno, Sarah Bigi, Serena Barello, Enrico Ferri Grazzi, Marco Follino, Maria Francesca Mansueto, Mariasanta Napolitano, Rita Carlotta Santoro, Giancarlo Castaman
Institutions: Federico II University Hospital, University of Naples Federico II, Università Cattolica del Sacro Cuore, University of Pavia, Fondazione Istituto Neurologico Nazionale Casimiro Mondino, Azienda Ospedaliera Universitaria Policlinico "Paolo Giaccone" di Palermo, University of Palermo, Azienda Ospedaliero-Universitaria "Renato Dulbecco", Azienda Ospedaliero-Universitaria Careggi
Language: English

Topic: Hemophilia Treatment and Research
Subfield: Hematology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: hybrid
Estimated APC paid: $4,760

Funders: Amgen, Sanofi, CSL Behring, Novo Nordisk, Swedish Orphan Biovitrum, Sanofi Genzyme
OpenAlex ID: W4415500500
FWCI:
Cites: 10
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