Work

Pharmacokinetic and Pharmacodynamic Evaluation of Bidridistrogene Xeboparvovec in an Aged Murine Model of Limb-Girdle Muscular Dystrophy Type 2E/R4

Year: 2025

Type: article

Source: Human Gene Therapy

DOI: 10.1177/10430342251393700

Authors: Stephen Baine, Jared Cui, Young-Eun Seo, Amber Kempton, Oliver Rogers, Alex Haile, Kaitlin Adegboye, Jasmine Wu, Luke Lemmerman, Mariana Guerrero, Caitlin Jones, Hannah Mayes, Tesla Freehafer, Sarah Lewis, Eric Pozsgai, Lilly East, Louise Rodino-Klapac, Rachael Potter

Institution: Sarepta Therapeutics (United States)

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

Funder: Sarepta Therapeutics

OpenAlex ID: W4415950815

FWCI:

Cites: 22

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