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Engasertib versus Placebo for Bleeding in Hereditary Hemorrhagic Telangiectasia

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Year: 2025
Type: article
Study designs: Randomized Controlled Trial, Clinical Trial
Source: New England Journal of Medicine
DOI: 10.1056/nejmoa2504411
Authors: Hanny Al-Samkari, Josefien Hessels, Antoni Riera-Mestre, Sophie Dupuis-Girod, Thibaut Van Zele, Vicente Gómez del Olmo, Pamela G. Hodges, Raquel Torres-Iglesias, Roberto Bertè, Pierre Saint-Mezard, Hedvika Lazar, Nicholas Benedict, Debra Barker, Corrado Bernasconi, Damien Picard, Elisabetta Buscarini, Hans-Jurgen Mager
Institutions: Harvard University, Massachusetts General Hospital, St. Antonius Ziekenhuis, Bellvitge University Hospital, Institut d'Investigació Biomédica de Bellvitge, Inserm, Commissariat à l'Énergie Atomique et aux Énergies Alternatives, CEA Grenoble, Hôpital Femme Mère Enfant, Hospices Civils de Lyon, Université Grenoble Alpes, Ghent University Hospital, Instituto Ramón y Cajal de Investigación Sanitaria, Hospital Universitario Ramón y Cajal, Azienda Ospedaliera Ospedale Maggiore, Aziende Socio Sanitarie Territoriale di Crema
Language: English

Topic: Vascular Anomalies and Treatments
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4416712181
FWCI: 4.722
Cites: 32
Cited by: 9
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