Work

Bilateral retinal rescue through unilateral AAV8-CYP4V2 gene delivery in Bietti crystalline dystrophy

Year: 2025

Type: article

Source: Molecular Therapy — Methods & Clinical Development

DOI: 10.1016/j.omtm.2025.101618

Authors: Laura A. Jenny, Yao Li, Stephen H. Tsang

Institutions: NewYork–Presbyterian Hospital, Columbia University Irving Medical Center, Columbia University

Language: English

Topic: Retinal Development and Disorders

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: gold

Estimated APC paid: $3,900

Funders: Foundation Fighting Blindness, Research to Prevent Blindness, National Institutes of Health, National Eye Institute, Alcon Research Institute

Awards: G6382212690, Translational Gene Therapy for CNGB1 Retinitis Pigmentosa, G9000072492, G9000103476, G9000120498, G9000313720, Defining Barriers to Gene Therapy, Gene Editing and Silencing in Phototransduction

OpenAlex ID: W4416738284

FWCI: 0.301

Cites: 6

Cited by: 1

Related to: 10