Work

Polyclonal somatic gene rescue via uniparental disomy confers multilineage hematopoietic potential in treatment-independent patients with DBA syndrome

Year: 2025

Type: conference-abstract

Source: Blood

DOI: 10.1182/blood-2025-746

Authors: Masanori Yoshida, Senthil Bhoopalan, Tsutomu Toki, Rika Kanezaki, Lili Kotmayer, Michelle Boals, Damian Krzyzanowski, Nishi Harwani, Paola Quarello, Ugo Ramenghi, Saskia Langemeijer, Ilja Diets, Kiminori Terui, Jason Farrar, Nathan Gray, Etsuro Ito, Marcin Wlodarski

Institutions: St. Jude Children's Research Hospital, National Center For Child Health and Development, Hirosaki University, Ospedale Regina Margherita, Radboud University Medical Center, Arkansas Children's Research Institute, University of Arkansas for Medical Sciences

Language: English

Topic: Blood disorders and treatments

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4417004539

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Cited by: 1

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