Lentiviral hematopoietic stem and progenitor cell gene therapy for Wiskott-Aldrich Syndrome: Early access experience in Italian patients based on 648/1996 law
Year: 2025
Type: conference-abstract
Source: Blood
Authors: Sabina Cenciarelli, Stefania Giannelli, Federico Fraschetta, Carmen Caputo, Davide Sala, Ketty Sinigaglia, Mariam Datukishvili, Elena Tomasetto, Francesca Ciotti, Maddalena Fraschini, Federica Salerio, Camilla Ferri, Federica Barzaghi, Valeria Calbi, Daniele Canarutto, Giulia Consiglieri, Matteo Doglio, Francesca Fumagalli, Vera Gallo, Maddalena Migliavacca, Salvatore Recupero, Francesca Tucci, Maria Ester Bernardo, Maria Pia Cicalese, Federica Miotto, Alessandro Aiuti, Francesca Ferrua
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4417006129
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