Work

Decoding Transgene Silencing from Stably Maintained AAV Genomes in Human Liver: Epigenetic Insights to Guide Next-Generation Vector Design

Year: 2025

Type: conference-abstract

Source: Blood

DOI: 10.1182/blood-2025-4310

Authors: Giulia Simini, Jenny McIntosh, Vincent Muczynski, Malo Journou, Paul Batty, Pratima Chowdary, Christopher Morton, Andrew Davidoff, Amit Nathwani

Institutions: The Royal Free Hospital, University College London, Inserm, St. Jude Children's Research Hospital

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W4417006290

Cites:

Cited by:

Related to: