Efficacy of mitapivat in patients with transfusion-dependent alpha-thalassemia: Subgroup analysis from the ENERGIZE-T trial
Year: 2025
Type: conference-abstract
Source: Blood
Authors: Ashutosh Lal, Andreas Glenthøj, Hanny Al-Samkari, Maria Domenica Cappellini, Kevin Kuo, Khaled Musallam, Sujit Sheth, Ali Taher, Lauren Czapla, Jeremie Estepp, Keely Gilroy, Hui Shao, Ferras Alashkar, Manuela Balocco, Bart Biemond, Anita Rijneveld, Adisak Tantiworawit, Nattiya Teawtrakul, Noppacharn Uaprasert, Efthymia Vlachaki, Antonis Kattamis, Vip Viprakasit
Institutions: UCSF Benioff Children's Hospital, Copenhagen University Hospital, Rigshospitalet, Harvard University, Massachusetts General Hospital, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, American University of Beirut Medical Center, American University of Beirut, Khalifa University of Science and Technology, Cornell University, Weill Cornell Medicine, Agios Pharmaceuticals (United States), Essen University Hospital, University of Duisburg-Essen, Ente Ospedaliero Ospedali Galliera, Amsterdam University Medical Centers, University of Amsterdam, Erasmus MC, Chiang Mai University, Khon Kaen University, Srinagarind Hospital, Faculty of Medicine, Khon Kaen University, Chulalongkorn University, Aristotle University of Thessaloniki, National and Kapodistrian University of Athens, Siriraj Hospital, Mahidol University
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4417009619
