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Long-term safety and efficacy of iptacopan in patients with paroxysmal nocturnal hemoglobinuria: 4- and 5-year follow-up of patients from Phase 2 studies who entered the roll-over extension program

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Year: 2025
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2025-3198
Authors: Antonio Risitano, Camilla Frieri, Bor-Sheng Ko, Lily Wong Lee Lee, Alexander Röth, Flore Sicre-de-Fontbrune, Eng Soo Yap, Sung-Soo Yoon, Philippe Ferber, Irina Baltcheva, Aurelie Verles, Silvia Sanz, Luca Monaco, Tim Costigan, Regis Peffault De Latour
Institutions: European Society for Blood and Marrow Transplantation, Azienda Ospedaliera S.Giuseppe Moscati, European Society for Blood and Marrow Transplantation, University of Naples Federico II, National Taiwan University, Queen Elizabeth Hospital, Essen University Hospital, University of Duisburg-Essen, Seoul National University Hospital, Novartis (Switzerland), Novartis (Spain), IQVIA (United States), Université Paris Cité, Assistance Publique – Hôpitaux de Paris
Language: English

Topic: Complement system in diseases
Subfield: Immunology
Field: Immunology and Microbiology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4417013775
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