Long-term safety and efficacy of iptacopan in patients with paroxysmal nocturnal hemoglobinuria: 4- and 5-year follow-up of patients from Phase 2 studies who entered the roll-over extension program
Year: 2025
Type: conference-abstract
Source: Blood
Institutions: European Society for Blood and Marrow Transplantation, Azienda Ospedaliera S.Giuseppe Moscati, European Society for Blood and Marrow Transplantation, University of Naples Federico II, National Taiwan University, Queen Elizabeth Hospital, Essen University Hospital, University of Duisburg-Essen, Seoul National University Hospital, Novartis (Switzerland), Novartis (Spain), IQVIA (United States), Université Paris Cité, Assistance Publique – Hôpitaux de Paris
Language: English
Subfield: Immunology
Field: Immunology and Microbiology
Domain: Life Sciences
Open Access status: closed
OpenAlex ID: W4417013775
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