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Cly-124, a first-in-class DCN1 inhibitor partially suppresses CUL3 neddylation and induces fetal hemoglobin is a new potential treatment for sickle cell disease

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Year: 2025
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2025-837
Authors: Sriram Krishnamoorthy, Samuel Miller, Anthony Monti, Enhua Zhou, Chi Hua Sarah Lin, Orna Lynch, Sayani Mukherjee, Cassie Hei, Robert Nicewonger, Colin Diner, Alejandra Macias-Garcia, Kristen Marino, Na Li, Ravi Ujjinamatada, Akshay Salegaonkar, Sunil Kuppasani, Maximilian Rogers-Grazado, Corey Hayford, Frank Lovering, Qin Tang, Emily Ye, Wei Zhang, Timothy Fulton, Jennifer O'Brien, Xiaoji Sun, Atli Thorarensen, Mauricio Cortes, Cameron Trenor
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4417015374
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