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Long-term mitapivat treatment improves inflammatory pro-fibrotic cardiomyopathy in a murine model of β-thalassemia.

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Year: 2025
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2025-727
Authors: Enrica Federti, Alessandra Ghigo, Tolunay Kavaz, Veronica Riccardi, Richard Pozzetto Huot, Jacopo Ceolan, Simone Villaboni, Angelo D'Alessandro, Federica Logrand, Leonardo Rivadeneyra, Megan Wind-Rotolo, Lucia De Franceschi
Institutions: University of Verona, University of Turin, University of Colorado Anschutz, Agios Pharmaceuticals (United States)
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4417016181
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