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The impact of voxelotor on the reduction in red blood cell transfusions in US patients with sickle cell disease

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Year: 2025
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2025-6530
Authors: Patricia Prince, Carmine Colavecchia, David Purdie, Emily Meier, Lili Jiang, Stella Chou, Ross Fasano, Christine Baker, John Shen, Thomas Zhen, Jeremy Rupon, Richard Drachtman
Institutions: Aetion (United States), Pfizer (United States), Children's Hospital of Philadelphia, University of Pennsylvania, Emory University, Rutgers, The State University of New Jersey, Rutgers Cancer Institute
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W4417020079
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