Preclinical evaluation of SPK-8011QQ, an adeno-associated virus gene therapy for people with hemophilia A leveraging the dirloctocogene samoparvovec platform encoding an activated Protein C-resistant B-domain deleted factor VIII
Year: 2025
Type: conference-abstract
Source: Blood
Authors: Nina Frey, Nicolas Receveur, Michel Enderlin-Paput, Emmeline Blanchard, Hayley Hanby, Julia Ramos, Tovo David
Language: English
Subfield: Hematology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4417021154