USA - CBER chief on remote work, CRISPR-Cas9, and rare disease gene therapy accelerated approval guidance
Year: 2024
Type: other
Abstract: The use of CRISPR-Cas9 gene editing technology has potential to transform the field of gene therapy through its simple and cost-effective delivery mechanism, said Peter Marks, director of the US Food and Drug Administration’s (FDA) Center for Biologics Evaluation and Research (CBER), during a 23 April webinar sponsored by the Alliance for a Stronger FDA. He also addressed FDA’s forthcoming guidance on accelerated approval for gene therapies for treating rare diseases. Marks also said that FD...
Source: OpenEdition (OpenEdition)
DOI: 10.58079/12f6t
Author: Vroby
Language: English
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
Open Access status: green
OpenAlex ID: W6899013025
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