UK – Responding to new final draft guidance from NICE for a new gene therapy for haemophilia B
Year: 2024
Type: other
Abstract: Professor Sir Stephen Powis, NHS National Medical Director, said: “This transformative gene therapy is the first of its kind for haemophilia B patients on the NHS and has the potential to significantly improve the lives of hundreds of people by helping to reduce symptoms such as painful bleeds. “It is a one-time therapy that could be truly life-changing for some, as it could help people avoid the need for regular hospital visits. “This promising drug is the latest in a series of pioneering g...
Source: OpenEdition (OpenEdition)
DOI: 10.58079/12ja4
Author: Vroby
Language: English
Subfield: Hematology
Field: Medicine
Domain: Health Sciences
Open Access status: green
OpenAlex ID: W6899047359
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