Work

Mannitol-facilitated CNS entry of rAAV2 vector significantly delayed the neurological disease progression in MPS IIIB mice

Year: 2009

Type: article

Source: Gene Therapy

DOI: 10.1038/gt.2009.85

Authors: D M McCarty, J DiRosario, K Gulaid, J Muenzer, H Fu

Institutions: Nationwide Children's Hospital, Abigail Wexner Research Institute, The Ohio State University, University of North Carolina at Chapel Hill

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: Sanfilippo Research Foundation, National Institute of Diabetes and Digestive and Kidney Diseases

Award: CNS Gene Therapy for Mucopolysaccharidosis IIIB w/ AAV

OpenAlex ID: W1978350886

FWCI: 4.346

Cites: 65

Cited by: 105

Related to: 10